Novel Approaches to Gene Therapies for Patients With Rare Genetic Diseases
Novel Approaches to Gene Therapies for Patients With Rare Genetic Diseases https://pediatricsnationwide.org/wp-content/themes/corpus/images/empty/thumbnail.jpg 150 150 Jessica Nye, PhD https://secure.gravatar.com/avatar/?s=96&d=mm&r=gAccording to the National Institutes of Health (NIH), nearly 7,400 diseases have been identified and classified as “rare” or “orphan” — “rare” because each afflicts fewer than 200,000 people in the United States and “orphan” because drug companies, unlikely to recoup research and development…
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