New Study Demonstrates Potential for a Gene Therapy for Vanishing White Matter Disease
New Study Demonstrates Potential for a Gene Therapy for Vanishing White Matter Disease https://pediatricsnationwide.org/wp-content/uploads/2024/06/Bradbury-Vanishing-White-Matter-Image-1024x552.jpg 1024 552 Katie Brind'Amour, PhD, MS, CHES https://pediatricsnationwide.org/wp-content/uploads/2021/03/Katie-B-portrait.gifThe research, conducted in mouse models, shows promising safety and efficacy for a currently incurable, life-limiting condition. Researchers at Nationwide Children’s Hospital have confirmed initial safety and efficacy data for a gene supplementation therapy for Vanishing White Matter (VWM) disease in mouse models. Testing multiple versions of therapy in two separate mouse models representing different…