Times of uncertainty offer an opportunity to reflect and reevaluate priorities.
Gene therapy shows promise for clinical benefit in demyelinating, neurodegenerative disease.
Novel disease-specific biomarkers are needed to improve prediction models in pediatric disease.
International program facilitates the diagnosis of a rare immunodeficiency in two children caused by a novel genetic variant.
Vedolizumab is a monoclonal antibody that targets α4β7 integrin present on gut homing T cells and is indicated for adult inflammatory bowel disease
Overlapping symptoms can cause delayed diagnosis of celiac disease in patients with cystic fibrosis.
Study of children who had reductions for developmental hip dysplasia at age 2 years or younger highlights differences in outcomes for open and closed reductions.
