Muscular Dystrophy

Endocrinology Considerations in Duchenne Muscular Dystrophy

While endocrinologists are not always part of a core DMD treatment team, their expertise is necessary, especially in handling the effects of long-term glucocorticoid therapy.

January 15, 2019 | Written by Jeb Phillips

Endocrinology, Muscular Dystrophy, Neurology

Big Gains in FSHD Research: A Newly Published Model of FSHD and a Potential Gene Therapy to Improve Functional Outcomes

The model aims to provide the basis for many future studies to bring therapeutic options to patients with FSHD.

November 16, 2018 | Written by Abbie Roth

Center for Gene Therapy, Muscular Dystrophy

Gene Therapy Continues to Show Promise for Limb-Girdle Muscular Dystrophy

Louise Rodino-Klapac, PhD, principal investigator in the Center for Gene Therapy, shares an update on the advancement of LGMD2E gene therapy to clinical studies.

June 13, 2017 | Written by Louise Rodino-Klapac, PhD

Center for Gene Therapy, Muscular Dystrophy