Researchers explore gene responses among SCD patients hospitalized for acute complications to inform understandings of the under-studied disease.
Research looking at mitochondrial targets in kidney health holds promise for cisplatin-induced kidney injury.
Clinical trials using gene therapy to boost the body’s production of clotting factor aim to remove the need for regular infusions — ideally giving patients years or even decades free from daily worry about their condition.
Researchers broaden the understanding chromatin architecture in human disease.
In a recent publication in Science Translational Medicine, researchers studied combinations of approved and investigational drugs to identify promising pairs, such as panobinostat and marizomib, for the treatment of diffuse intrinsic pontine glioma (DIPG) and other diffuse midline gliomas (DMG).
