Integration of experts from several subspecialties leads to more options for minimally invasive treatments for children and young adults with often debilitating lymphatic flow disorders.
International program facilitates the diagnosis of a rare immunodeficiency in two children caused by a novel genetic variant.
Vedolizumab is a monoclonal antibody that targets α4β7 integrin present on gut homing T cells and is indicated for adult inflammatory bowel disease
Researchers explore gene responses among SCD patients hospitalized for acute complications to inform understandings of the under-studied disease.
Research looking at mitochondrial targets in kidney health holds promise for cisplatin-induced kidney injury.
Clinical trials using gene therapy to boost the body’s production of clotting factor aim to remove the need for regular infusions — ideally giving patients years or even decades free from daily worry about their condition.
