DMD

FDA Approves Micro-dystrophin: A Small Gene With Big Promise
FDA Approves Micro-dystrophin: A Small Gene With Big Promise 1024 632 Abbie Miller

UPDATE: On June 22, 2023, the FDA announced accelerated approval for SRP-9001/ELEVIDYS for Duchenne muscular dystrophy (DMD) following decades of research in the Center for Gene Therapy at Nationwide Children’s Hospital. The FDA approved the treatment for pediatric patients 4-5 years old with DMD. Jerry Mendell, MD, principal investigator in the Center for Gene Therapy…